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The genetic defect - Adenosine deaminase (ADA) deficiency may be cured permanently by:
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- administering adenosine deaminase activators.
- introducing bone marrow cells producing ADA into cells at early embryonic stages.
- enzyme replacement therapy.
- periodic infusion of genetically engineered lymphocytes having functional ADA cDNA.
Correct Option: B
By introducing bone marrow cells producing ADA into cells at early embryonic stages, the genetic defect adenosine deaminase (ADA) deficiency may be cured permanently. It is due to mutation.